| Intrabone hematopoietic stem cell gene therapy for adult and pediatric patients affected by transfusion-dependent ß-thalassemia S Marktel, S Scaramuzza, MP Cicalese, F Giglio, S Galimberti, ... Nature medicine 25 (2), 234-241, 2019 | 225 | 2019 |
| Luspatercept improves hemoglobin levels and blood transfusion requirements in a study of patients with β-thalassemia A Piga, S Perrotta, MR Gamberini, E Voskaridou, A Melpignano, A Filosa, ... Blood, The Journal of the American Society of Hematology 133 (12), 1279-1289, 2019 | 133 | 2019 |
| Endocrine function and bone disease during long‐term chelation therapy with deferasirox in patients with β‐thalassemia major M Casale, S Citarella, A Filosa, E De Michele, F Palmieri, A Ragozzino, ... American journal of hematology 89 (12), 1102-1106, 2014 | 96 | 2014 |
| Treatment of hepatitis C virus infection with direct‐acting antiviral drugs is safe and effective in patients with hemoglobinopathies R Origa, ML Ponti, A Filosa, A Galeota Lanza, A Piga, GM Saracco, ... American journal of hematology 92 (12), 1349-1355, 2017 | 44 | 2017 |
| Luspatercept for the treatment of anaemia in non-transfusion-dependent β-thalassaemia (BEYOND): a phase 2, randomised, double-blind, multicentre, placebo-controlled trial AT Taher, MD Cappellini, A Kattamis, E Voskaridou, S Perrotta, AG Piga, ... The Lancet Haematology 9 (10), e733-e744, 2022 | 35 | 2022 |
| A study of the geographic distribution and associated risk factors of leg ulcers within an international cohort of sickle cell disease patients: the CASiRe group analysis C Antwi-Boasiako, B Andemariam, R Colombatti, EV Asare, C Strunk, ... Annals of hematology 99, 2073-2079, 2020 | 30 | 2020 |
| Effects of germline VHL deficiency on growth, metabolism, and mitochondria S Perrotta, D Roberti, D Bencivenga, P Corsetto, KA O’Brien, M Caiazza, ... New England Journal of Medicine 382 (9), 835-844, 2020 | 27 | 2020 |
| Clinical outcome of transfusions with extended red blood cell matching in β-thalassemia patients: a single-center experience A Belsito, D Costa, S Signoriello, C Fiorito, I Tartaglione, M Casale, ... Transfusion and Apheresis Science 58 (1), 65-71, 2019 | 26 | 2019 |
| Gene therapy for Beta thalassemia: preliminary results from the PHASE I/II Tiget-Bthal trial of autologous hematopoietic stem cells genetically modified with GLOBE lentiviral … S Marktel, MP Cicalese, F Giglio, S Scaramuzza, V Calbi, M Casiraghi, ... Blood 130, 355, 2017 | 21 | 2017 |
| Brain iron content in systemic iron overload: A beta-thalassemia quantitative MRI study R Manara, S Ponticorvo, I Tartaglione, G Femina, A Elefante, C Russo, ... NeuroImage: Clinical 24, 102058, 2019 | 19 | 2019 |
| Luspatercept increases hemoglobin, decreases transfusion burden and improves iron overload in adults with beta-thalassemia AG Piga, I Tartaglione, R Gamberini, E Voskaridou, A Melpignano, ... Blood 128 (22), 851, 2016 | 18 | 2016 |
| Brain functional impairment in beta‐thalassaemia: the cognitive profile in Italian neurologically asymptomatic adult patients in comparison to the reported literature I Tartaglione, R Manara, M Caiazza, PA Carafa, V Caserta, T Ferrantino, ... British journal of haematology 186 (4), 592-607, 2019 | 17 | 2019 |
| Long‐term improvement in cardiac magnetic resonance in β‐thalassemia major patients treated with deferasirox extends to patients with abnormal baseline cardiac function M Casale, A Filosa, A Ragozzino, G Amendola, D Roberti, I Tartaglione, ... American Journal of Hematology 94 (3), 312-318, 2019 | 17 | 2019 |
| Hearing loss in beta-thalassemia: Systematic review I Tartaglione, R Carfora, D Brotto, MR Barillari, G Costa, S Perrotta, ... Journal of Clinical Medicine 11 (1), 102, 2021 | 16 | 2021 |
| Mortality in β-thalassemia patients with confirmed pulmonary arterial hypertension on right heart catheterization VM Pinto, KM Musallam, G Derchi, G Graziadei, M Giuditta, R Origa, ... Blood, The Journal of the American Society of Hematology 139 (13), 2080-2083, 2022 | 15 | 2022 |
| An analysis of racial and ethnic backgrounds within the CASiRe international cohort of sickle cell disease patients: Implications for disease phenotype and clinical research AD Campbell, R Colombatti, B Andemariam, C Strunk, I Tartaglione, ... Journal of racial and ethnic health disparities 8, 99-106, 2021 | 15 | 2021 |
| Risk factors for heart disease in transfusion-dependent thalassemia: serum ferritin revisited G Derchi, C Dessì, P Bina, MD Cappellini, A Piga, S Perrotta, I Tartaglione, ... Internal and Emergency Medicine 14, 365-370, 2019 | 15 | 2019 |
| No evidence of increased cerebrovascular involvement in adult neurologically‐asymptomatic β‐Thalassaemia. A multicentre multimodal magnetic resonance study I Tartaglione, C Russo, A Elefante, M Caiazza, M Casale, R Di Concilio, ... British journal of haematology 185 (4), 733-742, 2019 | 14 | 2019 |
| Risk factors for endocrine complications in transfusion-dependent thalassemia patients on chelation therapy with deferasirox: A risk assessment study from a multi-center nation … M Casale, GL Forni, E Cassinerio, D Pasquali, R Origa, M Serra, ... Haematologica 107 (2), 467, 2022 | 13 | 2022 |
| Renal safety under long-course deferasirox therapy in iron overloaded transfusion-dependent β-thalassemia and other anemias R Origa, A Piga, I Tartaglione, G Della Corte, GL Forni, A Bruederle, ... American journal of hematology 93 (7), 172-175, 2018 | 13 | 2018 |
